Immune Reconstitution

175. A clinical trial in Japan of retroviral-mediated gene transfer to bone marrow CD34+ cells as a treatment of adenosine deaminase (ADA)-deficiency

Technology / Clinical Trial / Gene Therapy / Biological Sciences / Bone marrow / Enzyme / Adverse Event / Adverse Drug Reaction / Immune Reconstitution / Adenosine Deaminase / Molecular Targeted Therapy / Enzyme Replacement Therapy / Severe combined immunodeficiency / Gene Transfer / Enzyme / Adverse Event / Adverse Drug Reaction / Immune Reconstitution / Adenosine Deaminase / Molecular Targeted Therapy / Enzyme Replacement Therapy / Severe combined immunodeficiency / Gene Transfer
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